Márcia Cabedal Mata,  —

Recent Posts

• 6MWT With LOPD Patients May Depend Most on Age, Walker Use
• My Son’s First Evaluation at the Behavioral Health Clinic Goes Smoothly
• Atrophy-related Protein BNIP3 May Be New Target in LOPD
• My Son, Who Has Pompe Disease, Is About to Become a Brother
• Stem Cell Gene Therapy Blocks Anti-GAA Immune Response in Mice
• Exploring Different Mobility Devices for My Son, Who Has Pompe Disease
• Urinary Tract Problems May Be Common With IOPD, Despite ERT
• Weighing the Pros and Cons of Sending My Son Back to Preschool
• Switching to Nexviazyme Not So Easy for Infantile-onset Pompe
• Avrobio‘s AVR-RD-03 Gene Therapy Effective in Pompe Mouse Model