Treatment and Lifestyle
Living With Pompe
For people affected by Pompe disease, certain aspects of daily life may need to be adjusted to manage limitations, treatment regimens, and symptoms.
Pompe Treatment Options
While ERT is the only type of treatment approved to date for Pompe, supportive therapies can help maximize ability to function…
Enzyme Replacement Therapy and Enzyme Stabilizers
Enzyme replacement therapy (ERT) is the only treatment option approved for Pompe disease. Ways to enhance the action of ERT are being investigated, including the use of enzyme stabilizers that help stabilize the functional protein/enzyme and enhance its delivery to the tissues.
The ERT Process: Preparation, Treatment, and Aftercare
There are many things to consider before undergoing enzyme replacement therapy. Learn more about…