• Rare Disease Film Festival Highlights Patient and Researcher Unity
  • Study Finds Association Between Whole-body MRI Measurements and Muscle Function Scores
  • Caring for Your Heart When You Have Pompe Disease
  • Molecular ‘Tag’ Improves Efficacy of Gene Therapy for Pompe Disease in Mice, Study Shows
  • Enzyme Replacement Therapy Loses Effectiveness in Pompe Patients with Long-term Use, Study Suggests 
  • How Does Pompe Disease Affect Life Expectancy?
  • Active Ingredient of Blood Pressure Treatment Boosts ERT’s Efficacy in Skeletal Muscles, Mouse Study Suggests
  • Tips for Managing Stress When You Have Pompe Disease
  • Fluid Build-up in Newborn Could Be Sign of Infantile-onset Pompe, Case Study Says
  • Managing Breathing Problems in Late-onset Pompe Disease
  • AT-GAA Continues to Induce Motor, Lung Improvements in Pompe Adult Patients, Phase 1/2 Study Shows
  • Tips to Manage Stress for Pompe Disease Caregivers