• European Study: Myozyme Improves Walking, Respiratory Function in Adults With Pompe
  • Treatment Plan for Pompe Disease
  • MDA’s Virtual Drug Development Meeting Brings Together Pompe Patients, Industry
  • How Can an Enzyme Activity Test Help Diagnose Pompe Disease?
  • National Survey Seeks to Assess Full Social, Economic Burdens of Rare Diseases in US
  • Stem Cell Gene Therapy Restores Glycogen Levels, Aids Movement in Mouse Study
  • FAQs About Pompe Disease and Exercise
  • Myozyme at Higher Dose More Effective for Classic Infantile Pompe, Study Says
  • Mindfulness for Pompe Disease Caregivers
  • Glc4 Is Potential Biomarker of Pompe Disease, Study Suggests
  • Alexion Charitable Foundation Giving $1.1M to Assist Rare Disease Community During Pandemic
  • Prenatal Diagnosis for Pompe Disease