• Latest NORD Webinar Offers Insights on Starting Nonprofit, Patient Registry
  • AVR-RD-03 Gene Therapy Reduces Toxic Glycogen Buildup in Pompe Mouse Model
  • Eye Movement Condition Nystagmus May Be Feature of Infantile Pompe, Report Shows
  • Spoon Theory for Late-onset Pompe Disease Patients
  • NORD Hosting ‘RareLaunch’ Workshops to Help Start Rare Disease Non-profits
  • Whole-body MRI Finds Early Muscle Deterioration in Pompe Children, Study Shows
  • Newborn Screening for Pompe Disease
  • Bayer Acquires AskBio and its Gene Therapy Program for Pompe Disease
  • Feeding Tubes for Pompe Disease
  • UK Organization ‘Same But Different’ Announces ‘Glimmer of Hope’ Photo Contest Winner
  • Novel Mouse Model of Pompe Shows Potential of New Gene Therapy
  • Pompe Disease and Anesthesia