• NORD’s Advice on COVID-19: You’re Stronger Than You Think
  • NORD Partners with ‘Sing Me a Story’ for July 18–20 Living Rare Forum
  • I Have Pompe Disease; Will I Pass It Onto My Children?
  • Ultrasound May Help Assess Diaphragm Dysfunction in LOPD Patients
  • Global Rare Disease Group’s Focus: 1,000 New Therapies by 2027, Despite COVID-19
  • Small Molecule Improves Muscle, Heart Defects in New Zebrafish Model, Study Finds
  • Better Newborn Screening Needed for Pompe, Could Improve Prognosis, Report Says
  • Pediatric Rare Disease Therapies Increase, But Most Repurposed, Study Finds
  • Albuterol With ERT Improves Lung, Motor Function in LOPD Patients, Phase 1/2 Trial Shows
  • Video: BioNews’ Social Media Campaign Highlights #WhatMakesMeRare
  • Elsevier Opens Books, Review Articles to Rare Disease Researchers Starting Feb. 29
  • Advice on Starting Nonprofit Groups for Rare and Other Diseases Focus of NORD Webinar