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January 3, 2019 News by Alejandra Viviescas, PhD

First Late-Onset Pompe Disease Patient Treated With AT-GAA in Phase 3 Trial

Amicus Therapeutics has dosed the first patient in the Phase 3 PROPEL clinical trial that aims to compare investigational therapy AT-GAA (ATB200/AT221) to standard treatment in patients with late-onset Pompe disease. The trial (NCT03729362) is still recruiting patients. Throughout 2019, approximately 100 participants who have been previously…

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