Recent Posts
- 6MWT With LOPD Patients May Depend Most on Age, Walker Use
- My Son’s First Evaluation at the Behavioral Health Clinic Goes Smoothly
- Atrophy-related Protein BNIP3 May Be New Target in LOPD
- My Son, Who Has Pompe Disease, Is About to Become a Brother
- Stem Cell Gene Therapy Blocks Anti-GAA Immune Response in Mice
- Exploring Different Mobility Devices for My Son, Who Has Pompe Disease
- Urinary Tract Problems May Be Common With IOPD, Despite ERT
- Weighing the Pros and Cons of Sending My Son Back to Preschool
- Switching to Nexviazyme Not So Easy for Infantile-onset Pompe
- Avrobio‘s AVR-RD-03 Gene Therapy Effective in Pompe Mouse Model